Pipeline

Telomere Diseases

Candidates Indications Research Pre-IND IND Phase I/II Phase III Registration
EXG34217 Dyskeratosis Congenita*      
EXG34217 Fanconi Anemia*      
EXG34217 Aplastic Anemia          
EXG34217 Myelodysplastic Syndrome (MDS)          
Liver Cirrhosis          

Chromosome Diseases

Candidates Indications Research Pre-IND IND Phase I/II Phase III Registration
Down Syndrome (Trisomy 21)          
Edwards Syndrome (Trisomy 18)          
Patau Syndrome (Trisomy 13)          

Aging-Associated Diseases

Candidates Indications Research Pre-IND IND Phase I/II Phase III Registration
Immunological Aging          
Healthspan Extension          
Alzheimer's Disease          

Other Diseases

Candidates Indications Research Pre-IND IND Phase I/II Phase III Registration
Muscular Dystrophy