Our Pipeline
| Telomere Diseases | |||||||
|---|---|---|---|---|---|---|---|
| Candidates | Indication | Research | Pre-IND | IND | Phase I/II | Phase III | Registration |
|
EXG34217
Telomere Biology Disorders with Bone Marrow Failure (including Dyskeratosis Congenita) PhaseIND |
Telomere Biology Disorders with Bone Marrow Failure (including Dyskeratosis Congenita) | ||||||
| Chromosome Diseases | |||||||
|---|---|---|---|---|---|---|---|
| Candidates | Indication | Research | Pre-IND | IND | Phase I/II | Phase III | Registration |
|
Down Syndrome (Trisomy 21) PhaseIND |
Down Syndrome (Trisomy 21) | ||||||
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Edwards Syndrome (Trisomy 18) PhaseIND |
Edwards Syndrome (Trisomy 18) | ||||||
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Patau Syndrome (Trisomy 13) PhaseIND |
Patau Syndrome (Trisomy 13) | ||||||